Top Gene Therapy Startups


The Top Ten

1 Integrated Health Systems

Integrated Health Systems aims at dealing with fatal diseases like cancer and alzheimer's with their well equipped technologies and therapies. They focus on being with you in every step of your journey of fighting various diseases. - devinporter112

2 Moderna Therapeutics

Moderna Therapeutics, are pioneering the development of a new class of drugs made of messenger RNA (mRNA), this drug platform is build for the treatment of various diseases. - devinporter112

3 Editas Medicine

Editas Medicine's mission is to translate its genome editing technology into a novel class of human therapeutics that enable precise and corrective molecular modification to treat the underlying cause of a broad range of diseases at the genetic level. - devinporter112

4 Autolus

Autolus utilises advanced cell programming CAR-T and manufacturing technologies and have established a development-stage pipeline of products for the treatment of haematological malignancies and solid tumours. - devinporter112

5 Freeline Therapeutics

Freeline Therapeutics is a biopharmaceutical company specialising in developing liver directed gene therapies for bleeding disorders. - devinporter112

6 Translate Bio

Translate Bio is a leading mRNA therapeutics company developing a new class of potentially trans formative medicines to treat diseases caused by protein or gene dysfunction. - devinporter112

7 Precision BioSciences

Precision BioSciences is a genome editing company dedicated to improving life. The team seeks to solve not just treat, but solve significant problems in oncology, genetic disease, agriculture, and beyond via its proprietary ARCUS genome editing platform. - devinporter112

8 CytomX Therapeutics

CytomX is unlocking the potential of antibody therapeutics in oncology by developing a novel therapeutic antibody class of highly targeted Probody therapeutics. - devinporter112

9 Voyager Therapeutics

Voyager Therapeutics is a clinical stage gene therapy company developing life-changing treatments for severe diseases of the central nervous system. - devinporter112

10 Dimension Therapeutics

Dimension Therapeutics is developing novel, liver-directed gene therapy treatments for severe, rare genetic disorders. Dimension’s lead programs address significant medical needs for new therapies and include a wholly owned program in hemophilia B. - devinporter112

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